MOVING SICKLE CELL
RESEARCH FORWARD.

Patient Testimonials

The Clinical Study
I Participated in Changed My Life

3 min WATCH NOW

Ada Gonzalez lives with sickle cell disease and enrolled in a clinical study decades ago that she benefits from today.

The Clinical Study I Participated in Changed My Life

3 min WATCH NOW

Ada Gonzalez lives with sickle cell disease and enrolled in a clinical study decades ago that she benefits from today.

Updates

FDA Approves Novel Treatment to Target Abnormality in
Sickle Cell Disease

November 25, 2019

With Oxbryta, sickle cells are less likely to bind together and form the sickle shape, which can cause low hemoglobin levels due to red blood cell destruction. This therapy provides a new treatment option for patients with this serious and life-threatening condition.

Gene-Edited 'Supercells' Make Progress In Fight Against Sickle Cell Disease

November 19, 2019

Doctors are reporting the first evidence that genetically edited cells could offer a safe way to treat sickle cell disease, a devastating, incurable disorder that afflicts millions of people around the world.

FDA Approves First Targeted Therapy to Treat Patients with Painful Complication of Sickle Cell Disease

November 15, 2019

Today, the U.S. Food and Drug Administration approved Adakveo (crizanlizumab), a treatment to reduce the frequency of vaso-occlusive crisis – a common and painful complication of sickle cell disease that occurs when blood circulation is obstructed by sickled red blood cells – for patients age 16 years and older.

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Sending updates featuring new studies and other relevant information about emerging sickle cell treatment options.

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