Sickle Cell Disease Study Testimonials

My Contribution to Clinical Studies

3 mins WATCH NOW

Ada Gonzalez lives with sickle cell disease and enrolled in a clinical study decades ago that she benefits from today.

Making an Informed Decision As a Family

4 mins WATCH NOW

Jewel is a teenager living with sickle cell disease. She and her mother, Paula make informed decision about participating in clinical studies.


Novartis and the Bill & Melinda Gates Foundation collaborate to discover and develop an accessible in vivo gene therapy for sickle cell disease

February 17, 2021

Novartis today announced that it has entered into a grant agreement with the Bill & Melinda Gates Foundation.

What We’re Reading: Sickle Cell Gene Therapy Partnership; Global COVID-19 Cases on Decline; Storms Slow Vaccine Rollout

February 17, 2021

The Bill and Melinda Gates Foundation and Novartis are collaborating to discover and develop a one-step, one-time gene therapy treatment to cure sickle cell disease, STAT News reports.

Retinal Measures Potential Biomarkers for Sickle Cell Disease Progression

February 8, 2021

Results of a longitudinal prospective case-control study found rates of retinal thinning were higher among individuals with sickle cell retinopathy compared with individuals without the condition, and thinning rates increased as participants aged, and stages of retinopathy progressed.

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