Sickle Cell Disease Study Testimonials

My Contribution to Clinical Studies

3 mins WATCH NOW

Ada Gonzalez lives with sickle cell disease and enrolled in a clinical study decades ago that she benefits from today.

Making an Informed Decision As a Family

4 mins WATCH NOW

Jewel is a teenager living with sickle cell disease. She and her mother, Paula make informed decision about participating in clinical studies.


BCH-BB694 Gene Therapy Safely Treating Severe SCD Patients in Pilot Trial

January 14, 2021

BCH-BB694 — an experimental gene therapy targeting the BCL11A gene — safely increased the levels of fetal hemoglobin and prevented disease-associated complications in six people with severe sickle cell disease (SCD), according to interim data from a Phase 1 clinical trial.

Family shares importance of giving blood following Sickle Cell health scare

January 10, 2021

When it comes to treating those with Sickle Cell Anemia, we found that we can match blood beyond type down to a certain antigen and it turns out that 33% of African American donors have this antigen in their blood and almost 0% Caucasion donors have the antigen.

Deep Learning Model Detects Sea Fan Neovascularization in Patients With Sickle Cell Hemoglobinopathy

January 5, 2021

In an effort to detect sea fan neovascularization from ultra-widefield color fundus photographs (UWF-FPs) from patients with sickle cell hemoglobinopathy (SCH), researchers developed an automated system with high sensitivity and specificity, which holds potential to improve screening for vision-threatening proliferative sickle cell retinopathy.

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